Once-Rare Fungal Diseases Are Killing Millions in an Unprepared World
When most people think of dangerous infections, they picture bacteria or viruses. But for infectious disease specialists like ...
Scientists granted $420,000 to test gene therapy for rare neurological disease
Childhood-onset striatonigral degeneration is a rare genetic disorder that robs children of the ability to walk and speak by ...
TheHealthSite4h
Medical Breakthrough: 5-Yr-Old Becomes First In The World To Undergo Rare Bone Marrow Transplant
This first-of-its-kind case in the world was tricky to handle; the boy already suffered from preexisting health problems that ...
The National Institute for Health and Care Excellence4h
HST routing criteria: encouraging innovation in the treatment of ultra-rare diseases
Our chief medical officer, Professor Jonathan Benger, explains the crucial role the HST programme plays in encouraging ...
Live Science on MSN19h
In 'extremely rare' case, Michigan resident dies from rabies after receiving transplanted kidney carrying the virus
A Michigan resident has died from rabies following a kidney transplant at a hospital in Ohio. Investigations show that the ...
Retiring country music icon has rare disease. Here’s what we know
He took the stage and was great last week at the Grand Ole Opry’s 100th anniversary show, and now he is down to just two ...
Fairfax Co. teen turns rare disease diagnosis into youth-led support, advocacy
Khartik Uppalapati, 16, of Fairfax County, Virginia, has co-founded an advocacy group aimed at helping young people, like ...
Gene Hackman's wife was "super healthy" before tragic death-But a rare disease changed everything
Hollywood is mourning the shocking double tragedy of legendary actor Gene Hackman and his wife, Betsy Arakawa. While the 95-year-old Oscar winner was known to be battling dementia ...
STAT5d
Soleno Therapeutics’ ‘life-changing’ rare-disease drug approved
The FDA Wednesday approved the first drug to treat people with Prader-Willi syndrome, a rare genetic disease that causes an ...
An ‘Impossible’ Disease Outbreak in the Alps
In one tiny town, more than a dozen people were diagnosed with the rare neurodegenerative disease ALS. Why? I n March 2009, ...
Comprehensive insights into rare triglyceride disorder provided in new study
Triglycerides are a vital source of energy, but when levels become dangerously high, they can lead to serious health ...
US FDA expands approval for Alnylam's drug to treat rare heart disease
U.S. Food and Drug Administration approved Alnylam's drug to treat a rare and deadly heart disease on Thursday, allowing the ...