The prospects for a one-time treatment that reduces the risk of heart disease for the rest of a person’s life just got ...

When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

Additionally, improving CAR-T biological efficiency could reduce dosing needs, further cutting costs and expanding access.

The FDA granted regenerative medicine advanced therapy designation to ATSN-201, a gene therapy candidate for the treatment of ...

AMT-130 is administered through magnetic resonance imaging-guided, convection-enhanced stereotactic neurosurgical delivery into the striatum.

Gene therapy, with its offer of a possible cure for rare diseases like sickle cell, is losing early investors to ...

Gene therapy for cystic fibrosis is advancing fast. Explore key biotech players, clinical progress, and its potential to ...

Despite the challenges, including what CSL CEO Paul McKenzie has described as a fragmented U.S. healthcare system, the blood ...

A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular ...

UMass Chan Medical School has laid off or furloughed 200 employees, as the campus grapples with cuts to NIH research and ...

Gene therapy is an area of intensive research and development in the retina space, with promising prospects and significant challenges. The benefits and pitfalls of gene therapy were discussed by two ...

A team at the Centro Nacional de Investigaciones Cardiovasculares (CNIC) has developed an innovative gene-therapy strategy ...