The prospects for a one-time treatment that reduces the risk of heart disease for the rest of a person’s life just got ...

When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

AMT-130 is administered through magnetic resonance imaging-guided, convection-enhanced stereotactic neurosurgical delivery into the striatum.

UMass Chan Medical School has laid off or furloughed 200 employees, as the campus grapples with cuts to NIH research and ...

Shares of uniQure N.V. (NASDAQ:QURE) surged 39% following the announcement that the U.S. Food and Drug Administration (FDA) granted Breakthrough Therapy designation to AMT-130, its gene therapy ...

Thanks in part to federal funding for newborn hearing screening, about 98% of newborns are screened for hearing loss before ...

Scientists at the University of California, Riverside, have discovered how adult stem cells retain their regenerative power.

Research from Harvard Forest identified a crucial relationship between precipitation patterns and soil types in New England.

Roche gave an update this week about GENERATION HD2, testing the HTT-lowering drug tominersen in people with HD. The trial is ...