MyChesCo on MSN9h
FDA Unveils Key Updates on Rare Disease Advances, Food Safety, and Medical Innovations
The U.S. Food and Drug Administration (FDA) has released a series of announcements covering a wide range of initiatives and ...
Korea JoongAng Daily on MSN1h
When one doctor isn’t enough: How 'collective intelligence' is tackling rare childhood cancers
No single doctor can diagnose and treat every disease. For rare conditions like pediatric solid tumors, medical experts find ...
Retiring country music icon has rare disease. Here’s what we know
He took the stage and was great last week at the Grand Ole Opry’s 100th anniversary show, and now he is down to just two ...
STAT4d
Soleno Therapeutics’ ‘life-changing’ rare-disease drug approved
The FDA Wednesday approved the first drug to treat people with Prader-Willi syndrome, a rare genetic disease that causes an ...
An ‘Impossible’ Disease Outbreak in the Alps
In one tiny town, more than a dozen people were diagnosed with the rare neurodegenerative disease ALS. Why? I n March 2009, ...
Comprehensive insights into rare triglyceride disorder provided in new study
Triglycerides are a vital source of energy, but when levels become dangerously high, they can lead to serious health ...
BioPharma Dive10d
Biotech Community Curetopia Raises $1.77M to Advance Rare Disease Cures with Blockchain
In a groundbreaking achievement, Curetopia, the first Biotech Decentralized Autonomous Organization (DAO) built natively on ...
Rolling Out4d
Promising drug cuts Alzheimer’s risk by half in rare cases
Research shows experimental anti-amyloid drug reduced cognitive symptom risk by 50% in people with rare genetic mutations ...
BioPharma Dive4d
Epicrispr banks $68M to test epigenetic editing on rare muscle disease
The startup is using CRISPR tools to stop errant expression of a gene linked to facioscapulohumeral muscular dystrophy, a ...
Soleno jumps as analysts say US nod for rare disease drug transforms treatment options
Shares of Soleno Therapeutics jumped 40% in morning trading on Thursday, after the company's drug for a rare metabolic condition became the first such treatment to receive U.S. regulatory nod.
India Today on MSN2d
Rare disease drug makes human blood toxic to malaria-causing mosquitoes
Nitisinone, a drug used to treat rare diseases, can kill malaria-causing mosquitoes, a new study found. In a bid to fight malaria, researchers are coming up with new solutions to reduce the spike ...
Meet Daniela, the 12-year-old girl battling a rare disease who’s become the UConn women’s secret weapon
When the UConn women’s basketball team takes the court, they know that no matter what happens, they’ve got the support of one ...