When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

AMT-130 is administered through magnetic resonance imaging-guided, convection-enhanced stereotactic neurosurgical delivery into the striatum.

Scientists at the University of California, Riverside, have discovered how adult stem cells retain their regenerative power.

The prospects for a one-time treatment that reduces the risk of heart disease for the rest of a person’s life just got ...

CROs can contribute to site collaboration by also identifying and supporting non-academic institutions capable of conducting ...

A Ludwig Cancer Research study has identified a novel strategy for treating acute myelogenous leukemia (AML), an aggressive ...

The FDA granted regenerative medicine advanced therapy designation to ATSN-201, a gene therapy candidate for the treatment of ...

After exploring a rival buyout offer worth 50% more than its first, bluebird bio is back where it started. | After striking ...

Ten out of 11 kids who received gene therapy for a rare variant of congenital deafness enjoyed significant improvements when ...

New York University researchers say a simple, gene-based blood test has shown to be highly accurate in predicting whether ...

The Food and Drug Administration (FDA) has granted Fast Track designation to PBGENE-HBV, an investigational gene editing therapy for adults with chronic hepatitis B.

Sarepta (SRPT) shared updates from its clinical programs focused on limb-girdle muscular dystrophy subtypes 2C/R5, 2D/R3, and 2E/R4. Following ...