Researchers focused on Myotonic Dystrophy 1 heart problems are testing a novel approach to restore normal function. Myotonic Dystrophy Type 1 (DM1) is the most common adult-onset form of muscular ...

Patients with myotonic dystrophy face unique challenges in managing their health, from navigating complex care needs to overcoming barriers to physical activity. 1-2 Recent studies presented at ...

WASHINGTON (AP) — Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, sending company shares plummeting more than 25%.

Opens in a new tab or window Share on LinkedIn. Opens in a new tab or window A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...

The RESTORE VISION scientific team has identified seven rare ocular conditions that impact the cornea and the rest of the ocular surface. "With a comprehensive approach, we aim to restore the ...

Duchenne muscular dystrophy causes progressive muscle degeneration and weakness, but physical exercise should still be part of a comprehensive treatment strategy. Duchenne muscular dystrophy (DMD ...

Results also showed significant improvements in corneal staining and tear production, with effects observed as early as week 4 and maintained through week 12. Patients reported reduced reliance on ...

A new stem cell therapy has repaired blinding damage to the cornea in 93% of patients in an early clinical trial. However, severe injuries, such as those caused by chemical burns or infections ...

Novel stem cell therapy repairs 'irreversible' corneal damage in clinical trial Date: March 4, 2025 Source: Mass Eye and Ear Summary: Results from a phase 1/2 clinical trial of a novel stem cell ...

Please provide your email address to receive an email when new articles are posted on . Allogenic corneal inlays are highly biocompatible and easy to implant. They offer a simple, safe solution ...