The prospects for a one-time treatment that reduces the risk of heart disease for the rest of a person’s life just got ...

When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

AMT-130 is administered through magnetic resonance imaging-guided, convection-enhanced stereotactic neurosurgical delivery into the striatum.

Ten out of 11 kids who received gene therapy for a rare variant of congenital deafness enjoyed significant improvements when ...

Verve Therapeutics said Monday that initial data show that its investigational gene-editing therapy lowered cholesterol ...

A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular ...

Additionally, improving CAR-T biological efficiency could reduce dosing needs, further cutting costs and expanding access.

Gene therapy for cystic fibrosis is advancing fast. Explore key biotech players, clinical progress, and its potential to ...

CROs can contribute to site collaboration by also identifying and supporting non-academic institutions capable of conducting ...

Feb. 7, 2025 — A research team has made a major discovery on how the CUL5 gene affects CAR-T cell therapy, an advanced cancer therapy. The study reveals that reducing the activity of the CUL5 ...