Stocktwits

Ionis Pharmaceuticals Secures FDA Orphan Drug Designation For Rare Epilepsy Treatment

The treatment targets the SCN1A gene, which helps the brain produce a protein that controls electrical activity and prevents ...

Cardiff Oncology Receives FDA Orphan Drug Designation for Onvansertib in Chronic Myelomonocytic Leukemia

Cardiff Oncology, Inc. (Nasdaq: CRDF), a clinical-stage biotechnology company leveraging PLK1 inhibition to develop novel cancer therapies, today announced that the U.S. Food and Drug Administration ...
RTTNews

Cardiff's Onvansertib Wins FDA Orphan Drug Designation For Rare Blood Cancer

Cardiff Oncology, Inc. ( CRDF) on Wednesday said the U.S. Food and Drug Administration granted orphan drug designation to Onvansertib for chronic myelomonocytic leukemia.
PR Newswire

Xylyx Bio announces FDA Orphan Drug Designation and $2.99M NIH SBIR grant award for its lead organ graft product, Inspirex™ Lung

Xylyx Bio, Inc., a regenerative medicine company developing bioengineered technologies for organ transplantation, tissue ...
Fintel on MSN

Supernus Pharmaceuticals announces FDA recognition of seven years of orphan-drug exclusivity for ONAPGO

Supernus Pharmaceuticals, Inc., a biopharmaceutical company focused on developing and commercializing products for the treatment of central nervous system (CNS) diseases, announced that the U.S. Food ...

FDA Grants Orphan Drug Designation to Kedrion's QIVIGY® for Stiff Person Syndrome, an Ultra-Rare Neurological Disorder

Kedrion Biopharma announced that the U.S. Food and Drug Administration (FDA) has granted Orphan Drug Designation to Immune ...
Pulse 2.0

Xylyx Bio Receives FDA Orphan Drug Designation And $2.99 Million NIH Grant For Inspirex Lung

Xylyx Bio has received U.S. Food and Drug Administration Orphan Drug Designation for Inspirex Lung and a $2.99 million ...
Healio

FDA grants orphan drug designation to IKT-001 for PAH

Please provide your email address to receive an email when new articles are posted on . The FDA granted orphan drug designation to IKT-001 for treating patients with pulmonary arterial hypertension, ...
BioSpace

Vivacta Bio and Grit Bio Announce FDA Orphan Drug Designation for In Vivo CAR-T Therapy GT801 in Autoimmune Hemolytic Anemia

Co., Ltd. ("Vivacta Bio"), a company spun out of the in vivo CAR-T platform of Beijing Grit Biotherapeutics Co., Ltd. ("Grit ...
RTTNews

Tiziana Seeks FDA Orphan Drug Designation For Intranasal Foralumab

Foralumab is a fully human anti-CD3 monoclonal antibody being developed as an intranasal immunomodulatory therapy for neuroinflammatory and neurodegenerative diseases. When administered through the ...
streetinsider

RenovoRx receives FDA orphan drug designation for oxaliplatin

RenovoRx Inc. (NASDAQ: RNXT) announced that the U.S. Food and Drug Administration granted orphan drug designation for oxaliplatin in treating pancreatic cancer, according to a company statement. The ...